This tool is for research exploration only. It is not a medical device and does not provide medical advice. Drug candidates, evidence scores, and AI-generated content are not clinical recommendations. Always consult your medical team before making any treatment decisions.

Drug Candidates

22 candidates mapped to SDH-deficient disease pathways

Niraparib

Zejula

theoretical

PARP inhibitor (PARP1/2)

Sdh Driven Hrd
All SDH tumors
Evidence Score
45
FDA Approved
Erdafitinib

Balversa

theoretical

Pan-FGFR inhibitor (FGFR1/2/3/4), FDA-approved

Fgfr Signaling
GIST
Evidence Score
42
FDA Approved
Birabresib

OTX015, MK-8628

theoretical

BET bromodomain inhibitor (pan-BRD2/3/4)

Epigenetic Dysregulation
GIST
Evidence Score
33
1 trial
Pembrolizumab

Keytruda

theoretical

Anti-PD-1 monoclonal antibody (checkpoint inhibitor)

Hif Pdl1 Checkpoint EvasionSuccinate Immune Evasion
All SDH tumors
Evidence Score
32
FDA Approved2 trials
Capivasertib

Truqap

theoretical

Pan-AKT inhibitor (allosteric PH-domain binding; AKT1/2/3)

Mtor Pi3k Akt
PPGL/PCCGISTRCC
Evidence Score
32
FDA Approved1 trial
Panobinostat

Farydak

theoretical

Pan-HDAC inhibitor

Epigenetic Dysregulation
All SDH tumors
Evidence Score
30
FDA Approved1 trial
Palbociclib

Ibrance

theoretical

CDK4/6 inhibitor

Cdkn2a Cdk46 Cell CycleEpigenetic Dysregulation
GIST
Evidence Score
30
FDA Approved
Elimusertib

AZD7648

theoretical

DNA-PKcs inhibitor (DNA-dependent protein kinase catalytic subunit inhibitor)

Nhej Dnapk Backup RepairSdh Driven Hrd
All SDH tumors
Evidence Score
29
1 trial
Enasidenib

Idhifa

theoretical

IDH2 inhibitor

Epigenetic Dysregulation
All SDH tumors
Evidence Score
28
FDA Approved
Brequinar

DUP-785, NSC 368390

theoretical

DHODH inhibitor (dihydroorotate dehydrogenase inhibitor)

Pyrimidine Synthesis Vulnerability
All SDH tumors
Evidence Score
28
1 trial
Prexasertib

LY2606368

theoretical

CHK1/CHK2 kinase inhibitor

Chk1 Brcas Replication CheckpointSdh Driven Hrd
All SDH tumors
Evidence Score
28
2 trials
Peposertib

M3814

theoretical

DNA-PK (DNA-PKcs/PRKDC) inhibitor

Nhej Dnapk Backup RepairSdh Driven Hrd
All SDH tumors
Evidence Score
28
2 trials
Ganetespib

STA-9090

theoretical

HSP90 inhibitor (non-ansamycin resorcinol-based)

Hsp90 Hif Client ChaperoneHif Pseudohypoxia
All SDH tumors
Evidence Score
28
1 trial
RBS2418 (Uzaribat)
theoretical

ENPP1 inhibitor

Cgas Sting Innate ImmuneSdh Driven Hrd
All SDH tumors
Evidence Score
26
1 trial
Imetelstat

Rytelo

theoretical

Telomerase inhibitor (competitive TERT template antagonist)

Tert Telomerase Reactivation
PPGL/PCC
Evidence Score
25
FDA Approved1 trial
Ulevostinag

MK-1454

theoretical

Cyclic dinucleotide STING agonist (intratumoral)

Cgas Sting Innate ImmuneSdh Driven Hrd
All SDH tumors
Evidence Score
25
1 trial
Eflornithine (DFMO)

Iwilfin, Ornidyl

theoretical

ODC1 inhibitor (ornithine decarboxylase inhibitor / polyamine synthesis inhibitor)

Polyamine Metabolism
PPGL/PCC
Evidence Score
23
FDA Approved
Dichloroacetate (DCA)
theoretical

Pyruvate dehydrogenase kinase inhibitor

Hif PseudohypoxiaOxidative Stress Ros
All SDH tumors
Evidence Score
22
Epacadostat

INCB024360

theoretical

IDO1 inhibitor (indoleamine 2,3-dioxygenase 1 inhibitor)

Succinate Immune Evasion
PPGL/PCC
Evidence Score
22
1 trial
Teriflunomide

Aubagio

theoretical

DHODH inhibitor (active metabolite of leflunomide; FDA-approved)

Pyrimidine Synthesis Vulnerability
All SDH tumors
Evidence Score
22
FDA Approved1 trial
Plerixafor

AMD3100, Mozobil

theoretical

CXCR4 chemokine receptor antagonist

Hif Cxcr4 Chemokine MetastasisHif Pseudohypoxia
PPGL/PCC
Evidence Score
20
FDA Approved1 trial
Ascorbic Acid (High-dose IV)
theoretical

TET enzyme cofactor / α-KG-dependent dioxygenase activator

Epigenetic DysregulationOxidative Stress Ros
PPGL/PCC
Evidence Score
18